Cystic fibrosis remains an incurable genetic disorder that impairs lung function and significantly reduces life expectancy. A new combination drug therapy that addresses the disorder’s underlying defects offers a promising new treatment approach. The use of this therapy had previously been limited to adolescents and adults. Designed to meet the highest standards of clinical practice, a study co-led by Charité—Universitätsmedizin Berlin has now confirmed that this combination therapy regimen is also beneficial to primary school-aged children. Earlier treatment means disease progression is likely to be significantly slowed. The researchers’ findings have been published in the American Journal of Respiratory and Critical Care Medicine.
Cystic fibrosis: Causal treatment suitable from childhood
Cystic fibrosis remains an incurable genetic disorder that impairs lung function and significantly reduces life expectancy. A new combination drug therapy that addresses the disorder's underlying defects offers a promising new treatment approach. The use of this therapy had previously been limited to adolescents and adults. Designed to meet the highest standards of clinical practice, a study co-led by Charité—Universitätsmedizin Berlin has now confirmed that this combination therapy regimen is also beneficial to primary school-aged children. Earlier treatment means disease progression is likely to be significantly slowed. The researchers' findings have been published in the American Journal of Respiratory and Critical Care Medicine.